EDIT 103
Alternative Names: EDIT-103Latest Information Update: 15 May 2024
At a glance
- Originator Editas Medicine
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes - Retinitis pigmentosa
Highest Development Phases
- Preclinical Retinitis pigmentosa
Most Recent Events
- 08 May 2024 Editas Medicine initiates appeal of the Patent Trial and Appeal Board decision favouring Broad Institute for CRISPR patent interference in the USA
- 09 Jan 2023 EDIT 103 is available for licensing as of 09 Jan 2023. http://www.editasmedicine.com 9378305
- 13 Oct 2022 Pharmacodynamics data from a preclinical trial in retinitis pigmentosa released by Editas Medicine