DT 216
Alternative Names: DT 216P2; DT-216; Syn TEF1Latest Information Update: 27 May 2024
At a glance
- Originator Design Therapeutics
- Class Small molecules
- Mechanism of Action Frataxin expression stimulants; Genetic transcription modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Friedreich's ataxia