Research programme: genetic disorder therapeutics - Insmed
Latest Information Update: 27 Feb 2024
At a glance
- Originator Adrestia Therapeutics
- Class Cardiovascular therapies
- Mechanism of Action Undefined mechanism
- 
          
            
              Orphan Drug Status
              NoOrphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases. 
- New Molecular Entity Yes
Highest Development Phases
- Research Cardiomyopathies; Neurological disorders; Neuromuscular disorders
