Research programme: AAV gene therapies - Novarits
Latest Information Update: 05 Jan 2024
At a glance
- Originator Novartis
- Developer Novartis; Voyager Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Huntington's disease
- Research CNS disorders; Spinal muscular atrophy
Most Recent Events
- 02 Jan 2024 Voyager Therapeutics expands its capsid license agreement with Novartis to advance gene therapies for Huntington’s disease and Spinal muscular atrophy
- 02 Jan 2024 Preclinical trials in Huntington's disease in USA (Parenteral)
- 06 Mar 2023 Novartis exercises its option to license a of Next-Generation AAV Capsids for Neurological disorders