JR 479
Alternative Names: BBB-penetrating βHexosaminidase A (rDNA origin) - JCR Pharmaceuticals; JR-479; β-Hexosaminidase A - JCR PharmaceuticalsLatest Information Update: 06 Apr 2022
At a glance
- Originator JCR Pharmaceuticals
- Class Hexosaminidases; Recombinant proteins
- Mechanism of Action Hexosaminidase A replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical GM2 gangliosidoses