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Research programme: alpha-1 antitrypsin deficiency gene therapy - LENZ Therapeutics

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Drug Profile

Research programme: alpha-1 antitrypsin deficiency gene therapy - LENZ Therapeutics

Alternative Names: Research programme: AAT deficiency gene therapy - LENZ Therapeutics

Latest Information Update: 26 Mar 2024

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At a glance

  • Originator Graphite Bio
  • Developer LENZ Therapeutics
  • Class Gene therapies; Stem cell therapies
  • Mechanism of Action Cell replacements; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Research Alpha 1-antitrypsin deficiency

Most Recent Events

  • 21 Mar 2024 LENZ Therapeutics has merged with Graphite Bio to form LENZ Therapeutics
  • 21 Mar 2022 Early research in Alpha 1-antitrypsin deficiency in USA (Parenteral) (Graphite Bio pipeline, March 2022)

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