Sasineprocel
Alternative Names: A9-line dopamine neuron therapy - Aspen Neuroscience; ANPD-001Latest Information Update: 07 Aug 2026
At a glance
- Originator Aspen Neuroscience
- Class Induced pluripotent stem cell therapies
- Mechanism of Action Dopaminergic cell replacements
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Parkinson's disease
Most Recent Events
- 30 Jul 2026 Sasineprocel receives Regenerative Medicine Advanced Therapy (RMAT) status for Parkinson's disease in USA
- 11 Jun 2026 Aspen Neuroscience plans a phase III trial for Parkinson's disease
- 18 Mar 2026 Efficacy data from a phase I/II trial in Parkinson's disease released by Aspen Neurosciences