Research programme: small molecule therapeutics - Sionna Therapeutics
Alternative Names: Cystic fibrosis therapeutics - Sionna TherapeuticsLatest Information Update: 23 Jul 2024
At a glance
- Originator Sionna Therapeutics
 - Class Antifibrotics; Small molecules
 - Mechanism of Action Cystic fibrosis transmembrane conductance regulator modulators
 
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              Orphan Drug Status
              No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
 - New Molecular Entity Yes
 
Highest Development Phases
- Preclinical Cystic fibrosis