Research programme: small molecule therapeutics - Sionna Therapeutics
Alternative Names: Cystic fibrosis therapeutics - Sionna TherapeuticsLatest Information Update: 28 May 2026
At a glance
- Originator Sionna Therapeutics
- Class Antifibrotics; Small molecules
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Cystic fibrosis
Most Recent Events
- 28 May 2026 No recent reports of development identified for preclinical development in Cystic-fibrosis in USA
- 16 Jul 2024 Pharmacodynamics data from a preclinical trial in Cystic fibrosis released by Sionna Therapeutics
- 08 Jun 2023 Pharmacodynamics data from preclinical studies in Cystic fibrosis released by Sionna Therapeutics