PRAX 080
Alternative Names: PRAX-080Latest Information Update: 24 May 2022
At a glance
- Originator Praxis Precision Medicines
- Class Antiepileptic drugs; Antisense oligonucleotides
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Epilepsy