MYR 103
Alternative Names: MYR-103; Pelizaeus-Merzbacher Disease programme - MyrtelleLatest Information Update: 07 Jun 2022
At a glance
- Originator Myrtelle
- Class MicroRNAs
- Mechanism of Action RNA interference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Leukoencephalopathies
Most Recent Events
- 07 Jun 2022 MYR 103 is available for licensing as of 07 Jun 2022. https://myrtellegtx.com/
- 19 May 2022 Myrtelle has patent protection for unique vector and gene sequences, routes of administration and methods of use (Myrtelle website, May 2022)
- 11 May 2022 Preclinical trial in Leukoencephalopathies in USA (Parenteral)