PBGENE HbE
Alternative Names: PBGENE-HbE; PBGENE-NVSLatest Information Update: 26 Jun 2022
At a glance
- Originator Precision Biosciences
- Class Antianaemics; Gene therapies
- Mechanism of Action Beta globulin replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Beta-thalassaemia; Sickle cell anaemia