Research programme: cystic fibrosis gene therapies - Carbon Biosciences
Latest Information Update: 28 Jun 2022
At a glance
- Originator Carbon Biosciences
- Class Gene therapies
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Cystic fibrosis