BRL 101
Alternative Names: BRL-101Latest Information Update: 25 Sep 2024
At a glance
- Originator BRL Medicine
- Class Gene therapies; Haematopoietic stem cells therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Beta-thalassaemia
- Preclinical Sickle cell anaemia
Most Recent Events
- 13 Jun 2024 Pooled efficacy and safety data from phase I/II trials in Beta-thalassaemia presented at the 29th Congress of the European Haematology Association (EHA-2024)
- 12 Mar 2024 BRL Medicine plans a clinical trial for Beta-thalassaemia (In adults, In adolescents, In children) in China (IV, Infusion) in December 2024 (NCT06298630)
- 08 Mar 2024 BRL Medicine plans a clinical trial for Sickle cell anaemia (In children, In adolescents, In adults) in China (IV, Infusion) (NCT06300723)