CTX 320
Alternative Names: CTX-320Latest Information Update: 10 Jan 2024
At a glance
- Originator CRISPR Therapeutics
- Class Cardiovascular therapies; Gene therapies
- Mechanism of Action Gene transference; Lipoprotein A expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Cardiovascular disorders
Most Recent Events
- 08 Jan 2024 Phase-I clinical trials in Cardiovascular disorders in Switzerland (Parenteral), prior to January 2024
- 11 Nov 2023 Pharmacodynamics data from a preclinical trial in Cardiovascular disorders presented at the American Heart Association Scientific Sessions (AHA-2023)
- 06 Nov 2023 CRISPR Therapeutics plans a clinical trial for Cardiovascular disorders (Parenteral), in the first half of 2024