BMRD 001
Alternative Names: BMRD-001Latest Information Update: 27 Jul 2022
At a glance
- Originator BIORCHESTRA
- Class RNA
- Mechanism of Action Iduronate sulfatase replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Mucopolysaccharidosis II
Most Recent Events
- 27 Jul 2022 Early research in Mucopolysaccharidosis II in South Korea (Parenteral) (BIORCHESTRA pipeline, July 2022)