Research programme : kidney disorders gene therapies - Purespring Therapeutics
Alternative Names: AAV based kidney disease therapeutics - Purespring TherapeuticsLatest Information Update: 07 Nov 2025
At a glance
- Originator Purespring Therapeutics
- Class Gene therapies; Urologics
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Kidney disorders