ALXN 2030
Alternative Names: ALXN-2030Latest Information Update: 04 Apr 2025
At a glance
- Originator Alexion AstraZeneca Rare Disease
- Class Small interfering RNA
- Mechanism of Action Complement C3 expression inhibitors; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase II Renal transplant rejection
Most Recent Events
- 07 Mar 2025 Phase-II clinical trials in Renal transplant rejection in South Korea (SC) (NCT06744647)
- 20 Dec 2024 Alexion Pharmaceuticals plans a phase II CONCORD trial for Renal transplant rejection in the US, Brazil, Canada, South Korea and Taiwan (SC) in March 2025 (NCT06744647)
- 22 Aug 2022 Preclinical trials in Unspecified in USA (SC) before August 2022