RM 001 - Reforgene Medicine
Alternative Names: RM-001 - Reforgene MedicineLatest Information Update: 25 Sep 2024
At a glance
- Originator Reforgene Medicine
- Class Cell therapies; Gene therapies; Haematopoietic stem cells therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Beta-thalassaemia
Most Recent Events
- 13 Jun 2024 Pooled efficacy and safety data from phase 0 and phase I/II trials in Beta-thalassaemia presented at the 29th Congress of the European Haematology Association (EHA-2024)
- 09 Dec 2023 Safety and efficacy data from a two phase 0 trials in Beta-thalassaemia presented at the at the 65th American Society of Hematology Annual Meeting and Exposition (ASH-Hem-2023)
- 08 Jun 2023 Safety and efficacy data from a two phase 0 trials in Beta-thalassaemia presented at the 28th Congress of the European Haematology Association (EHA-2023)