Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

ECUR 506

Next Previous
Drug Profile

ECUR 506

Alternative Names: ECUR-506; GTP-506; iECURE-OTC

Latest Information Update: 06 Sep 2026

Price :
$50 *
Note:
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator iECURE
  • Class Gene therapies
  • Mechanism of Action Gene transference; Ornithine carbamoyltransferase replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Ornithine carbamoyltransferase deficiency disease
  • New Molecular Entity No

Highest Development Phases

  • Phase I/II Ornithine carbamoyltransferase deficiency disease
  • Preclinical Citrullinemia
  • Research Phenylketonuria

Most Recent Events

  • 27 Aug 2026 Updated efficacy, pharmacodynamics and adverse events data from a phase I/II trial in Ornithine carbamoyltransferase deficiency disease released by iECURE
  • 10 May 2026 Early research in Phenylketonuria in USA (Parenteral) prior to May 2026 (iECURE Pipeline, May 2026)
  • 10 May 2026 Preclinical trials in Citrullinemia in USA (Parenteral) prior to May 2026 (iECURE Pipeline, May 2026)

You need to be a logged in or subscribed to view this content

Request demo (opens in a new window)
If your organization or you do not have a subscription, try one of the following: If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top