VTA 1100
Alternative Names: VTA-1100Latest Information Update: 04 Oct 2022
At a glance
- Originator Vita Therapeutics
- Class Gene therapies; Induced pluripotent stem cell therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Duchenne muscular dystrophy
Most Recent Events
- 28 Sep 2022 Preclinical trials in Duchenne muscular dystrophy in USA (Parenteral), prior to September 2022 (CureDuchenne Ventures pipeline September 2022)