Research programme: lysosomal channel 2 therapeutics - Autifony Therapeutics
Latest Information Update: 29 Oct 2025
At a glance
- Originator Autifony Therapeutics
- Class Antiparkinsonians; Small molecules
- Mechanism of Action Ion channel modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Lysosomal storage diseases; Parkinson's disease
Most Recent Events
- 29 Oct 2025 Discontinued for Lysosomal storage diseases in United Kingdom (unspecified route), before October 2025 (Autifony Therapeutics pipeline, October 2025)
- 29 Oct 2025 Discontinued for Parkinson's disease in United Kingdom (unspecified route), before October 2025 (Autifony Therapeutics pipeline, October 2025)
- 06 Oct 2022 Early research in Lysosomal storage diseases in United Kingdom (Autifony Therapeutics pipeline, October 2022)