PGN EDO45
Alternative Names: PGN-EDO45Latest Information Update: 18 Nov 2022
At a glance
- Originator Pepgen Corporation
- Class Antisense oligonucleotides; Drug conjugates; Morpholines; Peptide drug conjugates
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Duchenne muscular dystrophy