Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

EDK 060

Next Previous
Drug Profile

EDK 060

Alternative Names: DTx-1252; EDK-060

Latest Information Update: 19 Jul 2023

Price :
$50 *
Note:
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator DTx Pharma
  • Developer Novartis
  • Class Small interfering RNA
  • Mechanism of Action PMP22 protein expression inhibitors; RNA interference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Charcot-Marie-Tooth disease
  • New Molecular Entity Yes

Highest Development Phases

  • Preclinical Charcot-Marie-Tooth disease

Most Recent Events

  • 17 Jul 2023 DTx Pharma has been acquired by Novartis
  • 07 Jun 2023 DTx 1252 receives Orphan Drug status for Charcot-Marie-Tooth disease in USA
  • 01 Nov 2022 Preclinical trials in Charcot-Marie-Tooth disease in USA (Parenteral) (DTx Pharma pipeline, November 2022)

You need to be a logged in or subscribed to view this content

Request demo (opens in a new window)
If your organization or you do not have a subscription, try one of the following: If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top