S 230815
Alternative Names: KCNT1 ASO; S-230815Latest Information Update: 29 Sep 2025
At a glance
- Originator Servier
- Class Antiepileptic drugs; Antisense oligonucleotides
- Mechanism of Action KCNT1 protein expression modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Epilepsy
Most Recent Events
- 18 Aug 2025 Servier plans a phase Ib/II KCNT1-DEE trial for Neurodevelopmental-disorders (In infants, In children, In adolescent) in France and US (Intrathecal) (CTIS2024-513332-17-00)
- 28 Nov 2023 Preclinical trials in Epilepsy in France (unspecified route) (Servier pipeline; November 2023)