GS 011
Alternative Names: GS-011Latest Information Update: 23 Jan 2023
At a glance
- Originator GenSight Biologics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene transference; NADH dehydrogenase subunit 1 replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Leber's hereditary optic atrophy
Most Recent Events
- 16 Dec 2022 Preclinical trials in Leber's hereditary optic atrophy in France (Intravitreal) (GenSight Biologics pipeline, December 2022)