Research programme: Duchenne muscular dystrophy antisense therapeutics - UGISense
Latest Information Update: 06 Jan 2023
Price :
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At a glance
- Originator UGISense
- Class Antisense elements; Peptide nucleic acids
- Mechanism of Action Dystrophin expression modulators; Gene silencing
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Duchenne muscular dystrophy
Most Recent Events
- 21 Dec 2022 Early research in Duchenne muscular dystrophy in Germany (Parenteral) before December 2022 (UGISense pipeline, December 2022)