PPI 1040
Alternative Names: PPI-1040Latest Information Update: 09 Jan 2023
At a glance
- Originator Med-Life Discoveries
- Class 1 ring heterocyclic compounds; Esters; Ethers; Omega 3 fatty acids; Plasmalogens
- Mechanism of Action Plasmalogen replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Rhizomelic chondrodysplasia punctata