Research programme: Charcot-Marie-Tooth disease antisense therapeutics - UGISense
Latest Information Update: 18 Jan 2023
At a glance
- Originator UGISense
- Class Antisense elements; Peptide nucleic acids
- Mechanism of Action Gene silencing; Myelin protein inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Charcot-Marie-Tooth disease
Most Recent Events
- 05 Jan 2023 UGISense has patent protection for its UgimersTM technology platform before January 2023 (UGISense pipeline, January 2023)
- 05 Jan 2023 Early research in Charcot-Marie-Tooth disease in Germany (Parenteral) before January 2023 (UGISense pipeline, January 2023)