Research programme: eye disorder therapeutics - Ascidian Therapeutics
Latest Information Update: 10 Nov 2023
At a glance
- Originator Ascidian Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Retinal disorders; Stargardt disease
Most Recent Events
- 08 Nov 2023 Ascidian Therapeutics announces intention to submit IND to US FDA for Retinal disorders, in early 2024
- 18 Apr 2023 Pharmacodynamics data from a preclinical trial in Retinal disorders released by Ascidian Therapeutics
- 04 Jan 2023 Preclinical trials in Stargardt disease in USA (Parenteral)