SION 719
Alternative Names: SION-719Latest Information Update: 16 Jun 2025
At a glance
- Originator Sionna Therapeutics
- Class Antifibrotics; Small molecules
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Cystic fibrosis
Most Recent Events
- 06 Jun 2025 Pharmacodynamics data from a preclinical study in Cystic fibrosis released in Sionna Therapeutics
- 04 Jun 2025 Sionna Therapeutics initiates enrolment in a phase I drug-drug interaction trial in Unknown location
- 20 Mar 2025 Adverse events and pharmacokinetics data from a phase I trial in Cystic fibrosis (In volunteers) released by Sionna Therapeutics