Research programme: genetic dilated cardiomyopathy therapeutics - Phlox Therapeutics/ Solid Biosciences
Latest Information Update: 17 Jan 2023
At a glance
- Originator Phlox Therapeutics; Solid Biosciences
- Class Cardiovascular therapies; Gene therapies; RNA
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Dilated cardiomyopathy