Haemophilia A gene therapy - Exegenesis Bio
Latest Information Update: 30 Jan 2023
At a glance
- Originator Exegenesis Bio
- Class Antihaemorrhagics; Gene therapies
- Mechanism of Action Factor VIII replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- Preclinical Haemophilia A
Most Recent Events
- 23 Jan 2023 Haemophilia A gene therapy - Exegenesis Bio is available for licensing as of 23 Jan 2023. https://exegenesisbio.com/partnering-business-development/#
- 23 Jan 2023 Preclinical trials in Haemophilia A in USA (Parenteral) Before January 2023 (Exegenesis Bio pipeline, January 2023)