UNC13A targeting antisense oligonuclotide therapeutic - AcuraStem
Latest Information Update: 06 Feb 2024
At a glance
- Originator AcuraStem
- Class Antisense oligonucleotides
- Mechanism of Action Nerve tissue protein modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Amyotrophic lateral sclerosis; Frontotemporal dementia