GBA1 gene therapy - Neurocrine Biosciences/ Voyager Therapeutics
Latest Information Update: 24 Apr 2024
Price :
$50 *
At a glance
- Originator Neurocrine Biosciences; Voyager Therapeutics
- Class Antiparkinsonians; Gene therapies
- Mechanism of Action Gene transference; Glucosylceramidase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Gaucher's disease; Parkinson's disease
Most Recent Events
- 16 Apr 2024 Voyager Therapeutics plans a clinical trial for Parkinson’s disease in 2025
- 16 Apr 2024 Voyager Therapeutics announces intention to file an Investigational New Drug (IND) application with the US FDA for Parkinson's disease in 2025
- 26 Feb 2024 Voyager Therapeutics expects to progressing GBA1 Parkinson’s disease towards clinical studies