HG 001
Alternative Names: HG-001Latest Information Update: 08 Feb 2023
At a glance
- Originator HuidaGene Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference; Survival of motor neuron 1 protein replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Spinal muscular atrophy
Most Recent Events
- 02 Feb 2023 Preclinical trials in Spinal muscular atrophy in China (unspecified route) before February 2023 (HuidaGene Therapeutics pipeline, February 2023)