RT 103
Alternative Names: RT-103Latest Information Update: 09 Mar 2023
At a glance
- Originator Regel Therapeutics
- Class Gene therapies
- Mechanism of Action Gene expression modulators; SYNGAP1 protein expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research CNS disorders
Most Recent Events
- 02 Feb 2023 Early research in CNS disorders in USA (Parenteral) (Regel Therapeutics pipeline, February 2023)