ART 020
Alternative Names: ART-020Latest Information Update: 03 Mar 2023
At a glance
- Originator ART BioScience
- Class Gene therapies; RNA
- Mechanism of Action Gene expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Duchenne muscular dystrophy
Most Recent Events
- 21 Feb 2023 Early research in Duchenne muscular dystrophy in Israel (Parenteral)