HMB 002
Alternative Names: HMB-002; HMB-VWFLatest Information Update: 30 Jun 2025
At a glance
- Originator Hemab
- Class Antibodies; Antihaemorrhagics; Bispecific antibodies; Recombinant proteins
- Mechanism of Action Factor VIIa modulators; Von Willebrand factor modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I/II Von Willebrand disease
Most Recent Events
- 24 Jun 2025 Adverse events and pharmacokinetics data from preclinical studies in Von Willebrand disease released by Hemab
- 24 Jun 2025 Adverse events, efficacy and pharmacokinetics data from a phase I/II trial in Von Willebrand disease released by Hemab
- 07 Feb 2025 Pharmacokinetics and pharmacodynamics data from preclinical trials in Von Willebrand disease released by Hemab