P PAH 101
Alternative Names: P-PAH-101Latest Information Update: 27 Feb 2023
At a glance
- Originator Poseida Therapeutics; Takeda
- Class Gene therapies
- Mechanism of Action Gene transference; Phenylalanine hydroxylase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Phenylketonuria