AL 00804
Alternative Names: AL-00804; AL-0804Latest Information Update: 19 Jul 2023
At a glance
- Originator AceLink Therapeutics
- Class Small molecules
- Mechanism of Action Glucosylceramide synthase inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Gaucher's disease; Lysosomal storage diseases
Most Recent Events
- 18 Jul 2023 AceLink Therapeutics plans a phase-I/II trial for Lysosomal storage diseases in 2024 (AceLink Therapeutics pipeline, July 2023)
- 06 Apr 2023 Pharmacodynamics and pharmacokinetic data from the preclinical studies in Gaucher disease released by AceLink Therapeutics
- 23 Feb 2023 Preclinical trials in Lysosomal storage diseases in USA (PO) before February 2023