VX 264
Alternative Names: VX-264Latest Information Update: 09 Apr 2025
At a glance
- Originator Vertex Pharmaceuticals
- Class Antihypercalcaemics; Stem cell therapies
- Mechanism of Action Pancreatic beta cell replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Type 1 diabetes mellitus
Most Recent Events
- 28 Mar 2025 Efficacy and adverse events data from a phase I/II trial in Type 1 diabetes mellitus released by Vertex Pharmaceuticals
- 16 May 2023 Vertex Pharmaceuticals initiates phase I/II clinical trial in Type 1 diabetes mellitus in Canada(Parenteral) (NCT05791201)
- 16 May 2023 Phase-I/II clinical trials in Type 1 diabetes mellitus in Switzerland, USA, United Kingdom, Italy, Germany and England (Parenteral)