Research programme: in vivo gene editing therapies - Mammoth Biosciences/Vertex Pharmaceuticals
Latest Information Update: 31 Mar 2023
At a glance
- Originator Mammoth Biosciences; Vertex Pharmaceuticals
 - Class Gene therapies
 - Mechanism of Action Undefined mechanism
 
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              Orphan Drug Status
              No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
 - New Molecular Entity No
 
Highest Development Phases
- Research Unspecified