RAG 17
Alternative Names: RAG-17Latest Information Update: 14 Sep 2024
At a glance
- Originator Ractigen Therapeutics
- Class Drug conjugates; Oligonucleotides; Small interfering RNA
- Mechanism of Action RNA interference; Superoxide dismutase 1 expression inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Phase 0 Amyotrophic lateral sclerosis
Most Recent Events
- 10 Sep 2024 US FDA clears Investigational new drug (IND) application for clinical trials
- 10 Sep 2024 Adverse events data from phase 0 trial in Amyotrophic lateral sclerosis released by Ractigen Therapeutics
- 15 May 2024 The Center for Drug Evaluation (CDE) of China's National Medical Products Administration (NMPA) approves the investigational new drug (IND) application for phase I clinical trial in Amyotrophic lateral sclerosis (ALS)