ESCAPE platform based therapeutics - Beam Therapeutics
Alternative Names: ESCAPE-Beam TherapeuticsLatest Information Update: 22 Mar 2023
At a glance
- Originator Beam Therapeutics
- Class Antianaemics; Gene therapies; Haematopoietic stem cells therapies
- Mechanism of Action Cell replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Beta-thalassaemia; Sickle cell anaemia
Most Recent Events
- 09 Mar 2023 Preclinical trials in Beta-thalassaemia in USA (Parenteral) prior to March 2023 (Beam Therapeutics website, March 2023)
- 09 Mar 2023 Preclinical trials in Sickle cell anaemia in USA (Parenteral) prior to March 2023 (Beam Therapeutics website, March 2023)