GMCN 508A
Alternative Names: GMCN-508ALatest Information Update: 10 Oct 2025
At a glance
- Originator Genmedicn Biopharma
- Developer Genmedicn Biopharma; The First Affiliated Hospital Of Guangxi Medical University
- Class Gene therapies; Haematopoietic stem cells therapies; Stem cell therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Alpha-thalassaemia
Most Recent Events
- 10 Oct 2025 GMCN 508A is still in phase I trials for Alpha-thalassaemia (In adolescents, In adults, In children) in China (Parenteral) (NCT05757245)
- 18 Apr 2023 Phase-I clinical trials in Alpha-thalassaemia (In adults, In children, In adolescents) in China (Parenteral) (NCT05757245)
- 10 Mar 2023 Preclinical trials in Alpha-thalassaemia in China (Parenteral) prior to March 2023