RPT 2950
Alternative Names: LINE-1; RPT-2950Latest Information Update: 05 Aug 2025
At a glance
- Originator ROME Therapeutics
- Class Skin disorder therapies
- Mechanism of Action RNA-directed DNA polymerase inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Clinical Phase Unknown Cutaneous lupus erythematosus; Dermatomyositis; Systemic lupus erythematosus
- Preclinical Autoimmune disorders
- Research Neurodegenerative disorders
Most Recent Events
- 27 Jun 2025 Preclinical development in Autoimmune disroders in China(unspecified route) (ROME Therapeutics pipeline, June 2025)
- 27 Jun 2025 Research in Neurodegenerative disorders in China (unspecified route) (ROME Therapeutics pipeline, June 2025)
- 27 Jun 2025 Clinical trials in Dermatomyositis, Cutaneous lupus erythematosus, Systemic lupus erythematosus, (unspecified route) (ROME Therapeutics pipeline, June 2025)