VSA 001
Alternative Names: VSA-001Latest Information Update: 04 Apr 2025
At a glance
- Originator Visirna Therapeutics
- Class Cardiovascular therapies; Small interfering RNA
- Mechanism of Action RNA interference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Cardiovascular disorders; Metabolic disorders
Most Recent Events
- 31 Dec 2023 Visirna Therapeutics completes phase I trial (In volunteers; In adults) in China (SC) (NCT05757596)
- 15 Jun 2023 Visirna Therapeutics plans a phase III trial for hyperlipoproteinaemia type I (In adults, In the elderly) in China (Injection) (NCT05902598)
- 17 May 2023 Visirna Therapeutics initiates enrolment in a phase I trial (In volunteers; In adults) in China (SC) (NCT05757596)