Drug Profile

AAV ATP7B gene therapy - MeiraGTx

Alternative Names: AAV-ATP7B gene therapy - MeiraGTx; AAV-ATP7B opti gene therapy - MeiraGTx

Latest Information Update: 30 Mar 2023

Price :

$50 ^*

Note:

Adis is an information provider. We do not sell or distribute actual drugs.
Final gross price and currency may vary according to local VAT and billing address.
Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

Originator MeiraGTx
Class Gene therapies
Mechanism of Action Copper-transporting ATPase replacements; Gene transference

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity No

Highest Development Phases

Preclinical Hepatolenticular degeneration

Most Recent Events

16 Mar 2023 Preclinical trials in Hepatolenticular degeneration in USA (Parenteral) prior to March 2023 (MeiraGTx pipeline, March 2023)
14 Dec 2022 Pharmacodynamics data from preclinical studies in Hepatolenticular degeneration released by MeiraGTx
02 Feb 2016 MeiraGtx files a PCT application for gene regulation platform worldwide

You need to be a logged in or subscribed to view this content Request demo

If your organization or you do not have a subscription, try one of the following:

Contacting your organization’s admin about adding this content to your AdisInsight subscription
Buying a PDF version of any individual profile
Request a free trial

If your organization has a subscription, there are several access options, even while working remotely:

Working within your organization’s network
Login with username/password or try to access via your institution
Persisted access using your organization’s identifier stored in your user browser for 90 days

For assistance, contact us at asktheexpert.adisinsight@springer.com