ABO 504
Alternative Names: ABO-504Latest Information Update: 04 Jun 2026
At a glance
- Originator Abeona Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action ATP binding cassette transporter subfamily A member 4 replacements; Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Stargardt disease
Most Recent Events
- 13 May 2026 Discontinued - Preclinical for Stargardt disease in USA (Intravitreous) (Abeona Therapeutics pipeline, May 2026)
- 18 Mar 2024 Abeona Therapeutics plans to submit IND to the US FDA for ABO 504
- 17 May 2023 Pharmacodynamics data from preclinical trials in Stargardt disease released by Abeona Therapeutics