ABO 504
Alternative Names: ABO-504Latest Information Update: 02 Apr 2024
At a glance
- Originator Abeona Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action ATP binding cassette transporter subfamily A member 4 replacements; Gene transference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Stargardt disease